Adeno-associated Virus Vectors for Gene Therapy

Written by well-known experts in this field. Adeno-associated virus used in gene therapy. The 10 chapters cover gene therapy in specific diseases such as hemophilia, kidney diseases, and disordes of the central nervous system.

* Presents a timely update of gene therapy using the adeno-associated virus
* Addresses gene therapy for hemophilia, kidney diseases, and disorders of the central nervous system
* Provides innovative advance on vector design
* Includes balanced treatment of theoretical risks of gene therapy

Topics include:
Overview of AAT gene therapy
Gene therapy for hemophilia and other blood disorders
Gene therapy for pulmonary disease
Gene therapy for retinal disease
Gene therapy for diabetes
Gene therapy for kidney disease
AAV disorders of the central nervous system
AAV cardiovascular disease applications
AAV and metabolic disorders